News Articles
Researchers Advance mRNA Delivery to the Retina Using Stabilized Lipid Carriers
Efficient delivery of synthetic mRNA to the retina remains one of the key hurdles in developing mRNA-based treatments for vision loss.
People Behind the Surgeries and the Lifesaving Procedures They Love
Surgeons, animals, owners — and two complex surgeries with joyful results
Progress toward a treatment for Krabbe disease (link is external)
In one out of 100,000 infants, a mutation in the GALC gene causes an incurable, always fatal disorder known as infantile Krabbe disease, or globoid cell leukodystrophy. Most children with…